For many stroke survivors, recovery is derailed by painful muscle stiffness and involuntary spasms that limit movement, independence, and quality of life. Often viewed as an unavoidable consequence of ...

Across the GCC, Novartis continues to expand in oncology, cardiovascular, renal and metabolic diseases, immunology, and ...

The former Little Mix star opened up about Ocean Jade and Story Monroe's spinal muscular atrophy diagnosis, but says she firmly believes they'll defy all the odds.

Biogen recorded declining sales for Spinraza in each of the four quarters of 2025, but the Massachusetts drugmaker sees ...

Treatment with a high-dose regimen of Spinraza safely improved motor function in children with SMA, according to data from ...

Researchers described what they believe to be the first case of SMA type 4 presenting with a false enlargement of a muscle in ...

The high-dose regimen of SPINRAZA (nusinersen) is approved in the European Union and Japan. The high-dose regimen is under review with the United States Food and Drug Administration (FDA) and has a ...

Her daughters have a rare condition.

PulseSight Therapeutics SAS, an ophthalmology clinical stage biotech company developing disruptive vectorized gene therapies with minimally-invasive delivery technology, announced the completion of ...

NEW YORK – Findings from two new clinical trials suggest that a form of gene therapy previously restricted to children under 2 years old can also benefit older children with spinal muscular atrophy ...

The MarketWatch News Department was not involved in the creation of this content. SCHAUMBURG, Ill., Nov. 26, 2025 /PRNewswire/ -- Cure SMA, the leading nonprofit organization dedicated to supporting ...

SCHAUMBURG, Ill., Nov. 26, 2025 /PRNewswire/ -- Cure SMA, the leading nonprofit organization dedicated to supporting those impacted by spinal muscular atrophy (SMA), welcomes the FDA approval of ...