Stuart Orkin and Swee Lay Thein shared a Breakthrough Prize in Life Sciences for their research on genetic causes of sickle ...
Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...
Dr. Marty Makary noted it had "record speed approval," the fastest approval of any gene therapy device combination in U.S.
Astellas Pharma has done some spring cleaning of its pipeline, dropping two phase 1 candidates and slamming the brakes on a ...
The agency's decision is based on results from a clinical trial in which the treatment improved hearing in 80 percent of the ...
Two studies led by the Chahrour Lab at UT Southwestern Medical Center shed new light on genes associated with autism spectrum ...
Intellia Therapeutics, a leading biotechnology company, announced that its CRISPR-based treatment for a rare swelling ...
The treatment, developed by Regeneron Pharmaceuticals, is for a very rare form of deafness. But it represents a medical ...
The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time ...
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