KJ Muldoon was diagnosed with a rare genetic disorder when he was born called severe CPS1 deficiency. KJ is one in a million babies that are diagnosed with this illness. Researchers and doctors used ...

When Nicole Muldoon and her husband Kyle learned their newborn son KJ had a deadly genetic condition, they were faced with an unimaginable choice: opt for a traditional but invasive liver transplant, ...

When you buy through links on our articles, Future and its syndication partners may earn a commission. In a world first, a baby in the U.S. received a personalized, CRISPR-based gene therapy that ...

A tailored CRISPR base-editing therapy was given for the first time to an infant who was born with a rare genetic disease, with promising effects, researchers reported. After the baby, named KJ, ...

A baby in Pennsylvania has become the first recipient of an experimental genetic therapy that targets a rare urea cycle disorder. The treatment, which involves customizing the gene editing process ...

An infant with a rare metabolic disease became the world’s first patient to be treated with a personalized CRISPR gene-editing treatment in a landmark study between Penn Medicine and the Children’s ...

Something was very wrong with Kyle and Nicole Muldoon’s baby. The doctors speculated. Maybe it was meningitis? Maybe sepsis? They got an answer when KJ was only a week old. He had a rare genetic ...

KJ Muldoon, the first infant to undergo gene-editing therapy, has accomplished another first as a 1-year-old — his first steps KJ is walking at home ahead of Christmas after being hospitalized last ...